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Pharmacology 3% exam weight

CNS Pharmacology — Sedative-Hypnotics, Antiepileptics, and Antipsychotics

Part of the NEET PG study roadmap. Pharmacology topic pharma-006 of Pharmacology.

CNS Pharmacology — Sedative-Hypnotics, Antiepileptics, and Antipsychotics

🟢 Lite — Quick Review (1h–1d)

Sedative-Hypnotics (Benzodiazepines & Z-drugs):

DrugHalf-lifeActive MetaboliteKey Use
DiazepamLong (20-100h)Yes (desmethyldiazepam)Status epilepticus, alcohol withdrawal
LorazepamIntermediateNoICU sedation, seizures
MidazolamShortNoPre-medication, induction
AlprazolamShortNoPanic disorder, anxiety
ZolpidemShort (~2.5h)NoInsomnia (non-BZD)

Antiepileptics — Monotherapy:

DrugMechanismKey Side EffectsNotes
PhenytoinNa+ channel blockGingival hyperplasia, hirsutism, peripheral neuropathyNon-linear kinetics
CarbamazepineNa+ channel blockAplastic anemia, SIADH, Stevens-JohnsonAuto-inducer
ValproateMultipleHepatotoxicity, teratogenicity, pancreatitisBroad spectrum
LevetiracetamSV2A modulationBehavioral changes, somnolenceNewer agent
PhenobarbitalGABA-A potentiationSedation, dependence, megaloblastic anemiaOldest AED

Antipsychotics:

  • Typical (First-gen): Haloperidol, Chlorpromazine, Fluphenazine
    • Side effects: Extrapyramidal symptoms (EPS), tardive dyskinesia, hyperprolactinemia
  • Atypical (Second-gen): Risperidone, Olanzapine, Quetiapine, Clozapine
    • Side effects: Metabolic syndrome (weight gain, DM2), sedation

🟡 Standard — Regular Study (2d–2mo)

GABA Receptor Pharmacology:

  • Benzodiazepines bind at α-γ interface of GABA-A receptor → ↑ Cl- channel opening frequency
  • Barbiturates bind at β subunit → ↑ Cl- channel opening duration
  • Key differences:
    • BZDs: anxiolytic, anticonvulsant, muscle relaxant, amnestic (allosteric modulators)
    • Barbiturates: same effects BUT no ceiling — respiratory depression risk is dose-dependent
    • BZD antagonist: Flumazenil
    • Barbiturate overdose: NO specific antagonist — support respiration

Benzodiazepine Pharmacology:

PropertyDiazepamLorazepamMidazolam
RoutePO, IV, IM, PRPO, IV, IMIV, IM, IN
OnsetFast (IV)IntermediateVery fast
Half-lifeLongIntermediateShort
Active metabolitesYesNoNo
Use in liver diseaseCautionPreferredPreferred

Barbiturate Pearls:

  • Phenobarbital: longest-used AED; also used in neonatal seizures
  • Thiopental: ultra-short acting; used for induction of anesthesia
  • Mephobarbital, pentobarbital: intermediate/sleep induction

Antiepileptic Mechanisms:

MechanismDrugsClinical Use
Na+ channel blockPhenytoin, Carbamazepine, Oxcarbazepine, Lamotrigine, TopiramateFocal seizures, tonic-clonic
Ca2+ channel block (T-type)Ethosuximide, ValproateAbsence seizures
GABA enhancementPhenobarbital, Benzodiazepines, Tiagabine, VigabatrinMultiple seizure types
Glutamate block (NMDA/AMPA)Topiramate, Felbamate, LamotrigineAdjunct therapy
SV2A modulationLevetiracetam, BrivaracetamAdjunct for focal/generalized

Antiepileptic Teratogenicity (NEET HIGH-YIELD):

  • Valproate — neural tube defects (spina bifida), facial dysmorphism, developmental delay → AVOID in pregnancy
  • Phenytoin — fetal hydantoin syndrome (craniofacial, nail hypoplasia)
  • Carbamazepine — neural tube defects (lower risk than valproate)
  • Lamotrigine — considered safer in pregnancy (but still requires folate)
  • B6 (folic acid) supplementation recommended for all women of childbearing age on AEDs

First-line AEDs by Seizure Type:

  • Focal onset: Carbamazepine, Lamotrigine, Levetiracetam
  • Generalized tonic-clonic: Valproate, Lamotrigine
  • Absence: Ethosuximide, Valproate (if comorbid generalized)
  • Myoclonic: Valproate, Levetiracetam
  • Status epilepticus: IV Lorazepam or IV Diazepam (if Lorazepam unavailable)

Dopamine Pathways & Antipsychotics:

PathwayEffect when blockedSymptoms
Mesolimbic↓ Positive symptomsHallucinations, delusions (THERAPEUTIC)
Mesocortical↑ Negative/cognitive symptomsFlat affect, anhedonia (WORSENING)
NigrostriatalExtrapyramidal symptomsParkinsonism, dystonia, akathisia
TuberoinfundibularHyperprolactinemiaGalactorrhea, amenorrhea, gynecomastia

EPS Side Effects (Nigrostriatal blockade):

EPS TypeOnsetFeaturesTreatment
Acute dystoniaHours-daysMuscle spasm (head, neck, eyes)Benztropine, diphenhydramine
AkathisiaDays-weeksInner restlessness, pacingBeta-blocker, benzodiazepine
ParkinsonismWeeks-monthsBradykinesia, rigidity, tremorAnticholinergics, amantadine
Tardive dyskinesiaMonths-yearsInvoluntary movements (orofacial)Stop drug ASAP; valbenazine, deutetrabenazine

Atypical vs Typical Antipsychotics:

FeatureTypical (Haloperidol)Atypical (Risperidone)
D2 selectivityHigh (mesolimbic + nigrostriatal)Moderate + 5-HT2A antagonism
EPS riskHighLower
Metabolic effectsLowerHigher (especially clozapine, olanzapine)
Negative symptomsMinimal benefitSome benefit
HyperprolactinemiaHighDose-dependent

Key Antipsychotic Drugs:

DrugUnique FeatureNotable Side Effects
HaloperidolFirst-line typical; high potencyEPS, QT prolongation
ClozapineGold standard for refractory schizophreniaAgranulocytosis (weekly WBC), myocarditis, metabolic
RisperidonePopular atypicalDose-dependent EPS, hyperprolactinemia
OlanzapineGood for agitationMarked weight gain, DM2, sedation
QuetiapineLow EPSSedation, metabolic (lower than olanzapine)
AripiprazolePartial D2 agonistActivation, less metabolic

Antidepressant Classes:

ClassMechanismSide EffectsExamples
TCANE + serotonin reuptake inhibitionAnticholinergic (dry mouth, constipation, urinary retention), cardiacAmitriptyline, imipramine
SSRISelective 5-HT reuptake inhibitionGI upset, sexual dysfunction, serotonin syndromeFluoxetine, sertraline, escitalopram
SNRI5-HT + NE reuptake inhibitionSimilar to SSRI + ↑ BPVenlafaxine, duloxetine
MAOIMonoamine oxidase inhibitionTyramine reaction (hypertensive crisis), serotonin syndromePhenelzine, tranylcypromine
AtypicalMixedVariableBupropion (seizure risk at high dose), mirtazapine (sedation, weight gain)

Serotonin Syndrome (SSRIs + MAOIs + meperidine, linezolid, methylene blue):

  • Features: Hyperthermia, muscle rigidity, hyperreflexia, autonomic instability, altered mental status
  • Treatment: Cyproheptadine (5-HT antagonist), cooling, ICU

🔴 Extended — Deep Study (3mo+)

Benzodiazepine Dependence & Withdrawal:

  • Chronic use → tolerance (especially sedation, not respiratory depression)
  • Abrupt cessation → withdrawal: anxiety, insomnia, tremor, seizures
  • Flumazenil — competitive antagonist at BZD binding site; used for BZD overdose
  • Zolpidem/zaleplon: non-BZD hypnotics; similar mechanism but shorter acting; some cross-reactivity with BZD receptors

Phenytoin Non-linear Kinetics (Michaelis-Menten):

  • At therapeutic doses: first-order kinetics
  • At toxic doses: zero-order (saturated metabolism)
  • Small dose increase → disproportionate plasma level increase
  • Saturable hepatic metabolism
  • Target therapeutic range: 10-20 μg/mL

Carbamazepine Auto-induction:

  • Induces own metabolism (CYP3A4, CYP2C9)
  • Plasma levels DECREASE over first few weeks of therapy
  • Also induces hepatic enzymes more broadly
  • Key interactions: ↓ OCPs, ↓ warfarin, ↓ many drugs

Levetiracetam & Brivaracetam:

  • SV2A protein modulation (synaptic vesicle glycoprotein)
  • Novel mechanism — fewer drug interactions
  • Broad-spectrum AED (focal and generalized seizures)
  • Behavioral side effects in children (irritability, mood changes)
  • No enzyme induction or inhibition

Clozapine Monitoring (REMS Program):

  • Weekly WBC/ANC monitoring (first 6 months), then biweekly, then monthly
  • Stop if ANC < 1000 or WBC < 3000
  • Risk of myocarditis, seizures (dose-dependent), metabolic syndrome
  • Reserved for treatment-resistant schizophrenia (failed 2 other antipsychotics)

Aripiprazole Mechanism:

  • Partial D2 agonist (not pure antagonist like typicals)
  • Partial 5-HT1A agonist + 5-HT2A antagonist
  • “Dopamine stabilizer” — blocks in hyperdopaminergic states, stimulates in hypodopaminergic states
  • Lower EPS and hyperprolactinemia compared to other atypicals
  • Activation side effects (akathisia, insomnia) in some patients

Antipsychotic Metabolic Monitoring (Atypical, especially Clozapine/Olanzapine):

  • Baseline + quarterly: weight, BMI, blood pressure, fasting glucose, lipids
  • Recommended: switch to lower-metabolic-risk agent if significant weight gain/DM

NEET PG Key Pearls:

  • Diazepam + lorazepam — preferred for status epilepticus (IV)
  • Ethosuximide — ONLY for absence seizures; NOT for other seizure types
  • Valproate — broad spectrum; teratogenic (neural tube defects); avoid in women of childbearing age unless absolutely necessary
  • Clozapine — only for refractory cases; agranulocytosis risk; requires WBC monitoring
  • Flumazenil — BZD antagonist; do NOT use in patients with seizure history on chronic BZDs (can precipitate seizures)
  • Serotonin syndrome — SSRIs + MAOIs or meperidine = contraindicated
  • EPS treatment — benztropine or diphenhydramine for acute dystonia; amantadine for parkinsonism
  • Tardive dyskinesia — stop offending drug immediately; consider tetrabenazine
  • Bupropion — contraindicated in eating disorders, seizure disorders (lowers seizure threshold)
  • Carbamazepine — induces hepatic enzymes; reduces OCP efficacy → use alternative contraception

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